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Next Gen Meds in SJIA 2016
Home > SJIA Foundation Events > Next Gen Meds in SJIA 2016

Next Gen Meds in SJIA 2016

Next Gen Meds in MAS, SJIA, NLRC4 mutation and related diseases

When:
Friday 21st of October: 6 PM
to
Sunday 23rd of October: 3 PM
Where:
Mandarin Oriental,
Washington DC.

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Focus

SJIA, MAS, Still’s Disease, NLRC4 mutation, MAS+ILD and related diseases. Goal is to identify next gen drug options for patients who are not controlled by current drugs.

Participants types:

  • Prominent Scientists focused on diseases listed above
  • Small group of parents of kids with diseases listed above
  • Scientists or representatives from drug companies
  • Regulators from USA and Europe

Conference Schedule & Reception

Day 0
 Oct 21th, Friday
Informal get together in the evening
Keynote talk: Eric Hoffman
Day 1
 Oct 22nd, Saturday 8.30 am to 5.30 pm
Patients panel: to understand patient perspective & need for next gen therapies

  • Talk by FDA: Clinical trials process in USA (with a focus on rare diseases in pediatrics)
  • Talk by EMA: Clinical Trial process in Europe (with a focus on rare diseases in pediatrics)
  • Talks on potential next gen drugs and therapies
  • IL-18 Binding Protein – Tadekinig Alpha
  • IL-17 Blocker – Secukinumab
  • IL1 Blockers – Anakinra updates
  • Interferon γ Blocker: NI-0501
  • Interferon α Blockers: Anifrolumab, Rontalizumab
  • Jak Inhibitors: Tofacitnib, Baricitnib
  • Jak Inhibitors: Ruxolitnib
  • Panel: Discussion of drugs presented in previous session
Day 2
 Oct 23rd, Sunday: 8.30 am to 3.00 pm
Breakfast session with patients: Focus group & Round Tables by investigators

  • Stem Cell Transplantation
  • Allogeneic Stem Cell Transplantation: Speakers from centers with recent experiences
  • Autologous Stem Cell Transplantation: Speaker from centers with recent experiences
  • Mesenchymal Stem Cell therapy: planned clinical trials in SJIA
  • Clinical Trials Round Table
  • Conference Wrap-up

Video & Presentation

SpeakerPresentation TitleVideo LinkPresentation Link
Dr. Hermine BrunnerWhat is SJIA and how is it different than other diseases?Video
Presentation
Dr. Esi MorganLeading Quality Improvements in Pediatric Rheumatology CareN/APresentation
Dr. Daniel LovellCurrent Clinical Trials in SJIA & MASVideoPresentation
Dr. Grant SchulertResearch Updates in SJIA & MASVideoPresentation
Dr. Alexei GromMacrophage Activation Syndrome in SJIAVideoPresentation
Dr. Jennifer HugginsTreating new and refractory SJIA patientsVideoPresentation
Parent PanelParents Panel Issues & Concerns of SJIA parentsVideoN/A
Doctor PanelSJIA Experts Answer Parent's QuestionsVideoN/A

Conference Organizers

Organized by the Systemic JIA Foundation, a privately funded foundation based in California. The foundation organizes conferences, conducts surveys, makes seed grants, working with researchers and parents to accelerate the search for a cure. This conference is inspired by drug-discovery conferences organized by other rare disease foundations which have successfully accelerated development of new therapies by bringing together patients, researchers, pharma and regulators.

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Systemic JIA Foundation

4 months ago

Systemic JIA Foundation
The SJIA / MAS working group in Europe has two great talks coming up on June 13th (10:30am -12 pm est). Event is free but you need to register: form.jotform.com/231316175510345Speakers are- Dr Pui Lee (Harvard) who will speak about mTor pathways in SJIA-Dr Randy Cron (UAB) who will speak about Hyperinflammation in HLH. #SJIA #Mas #pres See you there! ... See MoreSee Less

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Systemic JIA Foundation

4 months ago

Systemic JIA Foundation
www.youtube.com/watch?v=Vxoy5328MZcOldie but goldie. And kids enjoy this video too. This video from Cincinnati Children's is about angry macrophages in HLH but most of it applies to MAS as well. Also, it explains why Bone Marrow Transplants (BMT) can help. As some of you know, this treatment is increasingly being used in cases of refractory SJIA as well.#HLH #Mas #BMT #Macrophages ... See MoreSee Less

Max The Angry Macrophage | A Story about HLH | Cincinnati Children's

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www.cincinnatichildrens.org/hlhMeet Max, and learn about the rare immune disorder called hemophagocytic lymphohistiocytosis, better known as HLH. In ...

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Contact Us

Location 3584 Outlook Avenue, Cincinnati OH, 45208

Email Address info@systemicjia.org

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Disclaimer

This website is provided for educational and informational purposes only. Systemic JIA Foundation is not engaged in rendering medical advice or professional services and this information should not be used for diagnosing or treating a health problem. The site authors and the content providers make no representation or warranties, expressed or implied. Providing links to other websites does not imply that Systemic JIA Foundation endorses the information or services provided on those websites. The organizations operating those websites are solely responsible for the content found on their websites.