Here is the final program for the Next Gen therapies conference. Post a comment if you have any questions.
OCTOBER 21st, FRIDAY | |
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6.00pm:7.00pm | Drinks & Hors D̥oeuvres |
6.45pm:7.45pm | Welcome & Keynote talk by Eric Hoffman |
7.45pm:9.00pm | Dinner |
OCTOBER 22nd, SATURDAY | |
7.30am:8.30am | Breakfast |
8.35am:8.45am | Intro to conference (Rashmi) |
8:45am:9:10am | Patients panel: to understand patient perspective & need for next gen therapies |
9:10am:9:15am | Setting stage for next-gen drug discussion (Fabrizio De Benedetti) |
Session 1: IL-18 and Interferon Gamma | |
9.20am:9.50am | Targeting IL-18 (Scott Canna, Edward Behrens) |
9.50am:10.20am | Targeting Interferon Gamma (Alexei Grom, Fabrizio De Benedetti) |
10.20am:10.40am | Panel Discussion for Session 1 |
10.40am:11.00am | Break |
Session 2: IL-1 & IL-17 | |
11.00am:11.20am | Targeting IL-1 (Peter Nigrovic) |
11.20am:11.40am | Targeting IL-17 Blocker (Pierre Miossec) |
11.40am:12.00pm | Panel discussion for Session 2 |
12.00pm:1.30pm | Lunch |
Session 3: Jak STAT Pathway | |
1.30pm:1.50pm | Targeting Jak-STAT Pathway I (Adriana Alameida de Jesus) |
1.50pm:2.10pm | Targeting Jak-STAT Pathway II (Kim Nichols - remote talk) |
2.10pm:2.30pm | Panel discussion for Session 3 |
2.30pm:3.00pm | Open Mic ̐ 5 mins each for other targets not discussed today |
3.00pm:3.20pm | Break |
Session 4: Getting Clinical Trials & Expanded Access | |
3.20pm:3.35pm | Nuts & Bolts of clinical trials in rare pediatric diseases: EMA perspective (Richard Vesely) |
3.35pm:3.50pm | Nuts & Bolts of clinical trials in rare pediatric diseases: FDA perspective (FDA Rep) |
3.50pm:4.05pm | Nuts & Bolts of clinical trials in rare pediatric diseases: Pharma perspective (Cristina de Min) |
4.05pm:4.20pm | Expanded Access Programs (FDA Rep) |
4.20pm:5.30pm | Panel Discussion for Clinical trials / Expanded Access (moderated by Alexei Grom) |
6.30pm:7.00pm | Take cabs to dinner (Meet at 6.30 in hotel foyer) |
7.00pm:9.00pm | Dinner |
OCTOBER 23rd SUNDAY | |
7.30am:8.30am | Breakfast |
7.30am:8.30am | Mesenchymal Stem Cell Focus Groups (Patients & Nora Singer) |
8.30am:9.20am | Open time (for ad-hoc discussions) |
Session 5: Stem Cell Transplantation | |
9.20am:9.40am | Overview & Autologous transplantation in SJIA (Nico Wulffraat & Lucy Wedderburn - remote) |
9.40am:10.00am | Allogeneic Stem Cell Transplantation in SJIA (Paul Veys - remote talk) |
10.00am:10.20am | BMT in HLH (Rebecca Marsh) |
10.20am:10.40am | Break |
10.40am:11.40am | Panel Discussion of Stem Cell Transplantation (moderated by Nico Wulffraat) |
Session 6: Mesenchymal Stem Cells | |
11.40am:11.55am | MSCs in SJIA (Nico Wulffraat) |
11.55am:12.10pm | MSCs in SJIA: Plan for clinical trials (Nora Singer) |
12.10pm:12.30pm | Panel discussion of MSCs |
12.30pm:2.00pm | Lunch |
2.00pm-3.00pm | Session 7: Reflections and conference wrap up |
[…] a researcher in another childhood disease (Duchenne Muscular Dystrophy), gave the keynote at our next-gen SJIA treatments conference in October. He is leading an effort at Reveragen to bring a steroid replacement called Vamorolone […]